NXT007 prophylaxis in people with hemophilia A with or without FVIII inhibitors: A global Phase I/II multiple-ascending-dose study
Maria Elisa Mancuso, Davide Matino, Dan Hart, Francisco José López-Jaime, Christophe Schmitt, Sanjay Ahuja, Giuliana Ventriglia, Anna Kiialainen, Laura Young, Olivier Catalani, Mark Belletrutti, Tom Chu, Jerzy Windyga, Víctor Jiménez-Yuste, Michaela Lehle, Janice M. Staber
Session: Short Talks - Emerging Therapeutics and Prophylactic Strategies in Coagulation Disorder
- Short Talks (Live Event)
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Transaminase Elevations in the Fitusiran Clinical Development Program With the Antithrombin-Based Dose Regimen
Sanjay Ahuja, Savita Rangarajan, Chur-Woo You, Bulent Zulfikar, Abhimanyu Yarramaneni, Laurel A Menapace, Yuqian Shen, Steven W Pipe
Session: Posters/Exhibits/Break
- Posters/Exhibits/Break (On-Demand)
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Sex and age-based evaluation of a newly formulated intranasal DDAVP compared with intranasal DDAVP and subcutaneous DDAVP in type 1 von Willebrand disease
Sanjay Ahuja, Sweta Gupta, Magdalena Lewandowska, Jennifer Maahs, Sonia Nasr, Amy Shapiro
Session: Posters/Exhibits/Break
- Posters/Exhibits/Break (On-Demand)
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Evaluating pen-injector handling and PROs in patients switching from emicizumab to Mim8 in FRONTIER5
Johnny Mahlangu, Sanjay Ahuja, Erin Cockrell, Víctor Jiménez-Yuste, Michele Schiavulli, Amalie Rhode Høgh Nielsen, Camila Martins Mazini Tavares, Emily Waters, Cédric Hermans, Dan Johnson
Session: Posters/Exhibits/Break
- Posters/Exhibits/Break (On-Demand)
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From Efficacy to Experience: 52-Week Patient-Reported Outcomes with Mim8 in Adolescents and Adults with Hemophilia A with or without Inhibitors (FRONTIER2)
Cédric Hermans, Sanjay Ahuja, Hazza Alzahrani, Cihan Ay, Peter Kampmann, Samya Obaji, Sophie Susen, Ciprian Ionut Tomuleasa, Lize van Vulpen, Amalie Rhode Høgh Nielsen, Ilgiz Rakhmatullin, Emily Waters, Carmen Escuriola-Ettingshausen, Arjun Menon
Session: Posters/Exhibits/Break
- Posters/Exhibits/Break (On-Demand)
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